When Geography, Cost, and Policy Become as Life-Limiting as a Disease
Jul 23, 2026 - 00:36:20
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When Endpoints Miss the Point
Families of children with the ultra-rare mitochondrial disorder pyruvate dehydrogenase complex deficiency, or PDCD, are fighting to get the U.S. Food and Drug Administration to provide a path to approval Saol Therapeutic...
About This Episode
When Endpoints Miss the Point is an episode from RARECast by RARECast. Families of children with the ultra-rare mitochondrial disorder pyruvate dehydrogenase complex deficiency, or PDCD, are fighting to get the U.S. Food and Drug Administra...
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Published Mar 12, 2026, 00:36:47 long, audio available.
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