When Geography, Cost, and Policy Become as Life-Limiting as a Disease
Jul 23, 2026 - 00:36:20
Radio and PodcastLive Radio & PodcastsBusiness
Fitting Big Genes into Small Vectors
Many disease‑causing genes are too large to be packaged into standard AAV gene therapy vectors, leaving a long list of otherwise gene-therapy-ready conditions without viable treatments. SpliceBio is leveraging a protein...
About This Episode
Fitting Big Genes into Small Vectors is an episode from RARECast by RARECast. Many disease‑causing genes are too large to be packaged into standard AAV gene therapy vectors, leaving a long list of otherwise gene-therapy-ready conditions wit...
Podcast
This episode belongs to RARECast.
Listen Online
Use the player on this page to stream the episode online.
Episode Details
Published Jun 18, 2026, 00:33:24 long, audio available.
Related Episodes
Continue listening to more episodes from RARECast.
A One-Time Cell Therapy to Reset the Immune System in Autoimmune Diseases
Jul 16, 2026 - 00:36:49
Building the Infrastructure for Made‑to‑Order Gene Therapies
Jul 9, 2026 - 00:35:49
Rewiring the Rare Disease Diagnostic Odyssey
Jul 2, 2026 - 00:38:11
Emerging from a Life in the Shadows
Jun 25, 2026 - 00:36:36
Targeting Iron Dysregulation in the Neurodegenerative Condition MSA
Jun 11, 2026 - 00:33:09
Long Reads, Shorter Journeys
Jun 4, 2026 - 00:35:23
The Critical Role of Patient Community-Industry Partnership in Advancing a Gene Therapy
May 28, 2026 - 00:46:20