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Building the Infrastructure for Made‑to‑Order Gene Therapies
The case of baby KJ Muldoon, an infant born with a lethal genetic metabolic disorder, demonstrates the potential to compress years of therapeutic development into months using an in vivo base editing approach. Jeff Colle...
About This Episode
Building the Infrastructure for Made‑to‑Order Gene Therapies is an episode from RARECast by RARECast. The case of baby KJ Muldoon, an infant born with a lethal genetic metabolic disorder, demonstrates the potential to compress years of ther...
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Published Jul 9, 2026, 00:35:49 long, audio available.
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