Using AI and Longitudinal Data to Transform Rare Disease Care
May 7, 2026 - 00:19:21
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How a Foundation Built Its Own Drug Program for an Ultra-Rare Disease
Schaaf-Yang syndrome is an ultra-rare neurodevelopmental disorder that is closely related to but distinct from Prader-Willi syndrome. It typically presents from birth with poor muscle tone, feeding and breathing difficul...
About This Episode
How a Foundation Built Its Own Drug Program for an Ultra-Rare Disease is an episode from RARECast by RARECast. Schaaf-Yang syndrome is an ultra-rare neurodevelopmental disorder that is closely related to but distinct from Prader-Willi syndr...
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Published Mar 26, 2026, 00:35:50 long, audio available.
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