Science & Medicine

Rare Disease, Cell & Gene Therapy Monthly RoundUp

Partners4Access

A monthly podcast highlighting the most important news developments and its impact on the orphan drug, cell and gene therapy world. Visit

Episodes

20 of 108 episodes

Solving Patient Matching in Rare Disease Trials

One of the most persistent barriers in rare disease drug development isn’t the science — it’s identifying and reaching the small number of p...

00:33:36Apr 29, 2026

Rare Disease Day Special: The stats and stories you need to hear.

Rare Disease Day Special | Let’s Talk Rare This Rare Disease Day, Let’s Talk Rare releases a special episode focused on the data and real-wo...

00:32:20Feb 27, 2026

2026 Trends: A Year Of Change & Opportunity

26 isn’t just another year in market access — it’s a turning point. In this episode of Let’s Talk Rare , P4A dives into the trends that are...

00:17:08Jan 30, 2026

Going To Glasgow: ISPOR 2025

In this episode of Let’s Talk Rare , we looked back at P4A’s recent trip to Glasgow, where our colleagues, Sam Morrison & Iro Malekou were o...

00:22:15Dec 2, 2025

Conversations Beyond the Clinic

Recorded live from ESMO 2025, Conversations Beyond the Clinic explores the different perspectives of the attendees and stakeholders at the E...

00:26:18Nov 3, 2025

Voices Uncovered: Understanding Mental Health in Rare Diseases using Social Listening

In this episode, we tune into the unfiltered voices of patients and caregivers navigating life with rare conditions. Through the power of so...

00:30:05Sep 29, 2025

Stronger Together: Collaborating for Better Patient Information with Catherine Richards Golini

How do we make sure patients receive health information that is clear, trustworthy, and truly helpful? We sit down with Catherine Richards G...

00:33:16Aug 26, 2025

OST-HER2 and the Fight Against Osteosarcoma: A New Hope After 40 Years

Join us as we sit down with Paul Romness of OS Therapies to explore an exciting breakthrough in OST-HER2 targeted therapies for osteosarcoma...

00:27:44Jul 1, 2025

AI for Rare Disease: From Discovery to Trials, Smarter and Faster

Discover how artificial intelligence is transforming the future of rare disease research in the latest episode of Let’s Talk Rare , the offi...

00:37:48May 29, 2025

Improving Alignment In Drug Development

In the latest episode of Let's Talk Rare, Owen Bryant & Georgie Rack delve into the world of drug development in rare diseases. They are joi...

00:36:35Apr 28, 2025

Breaking Barriers

Brain cancers are notoriously difficult to manage with current treatments offering limited effectiveness. But what if there was a way to cha...

00:27:44Mar 31, 2025

P4A's 5 Top Trends for 2025

Dive into P4A's annual appraisal of the year ahead. In this episode of Let's Talk Rare we examine the most important trends as identified an...

00:27:22Jan 31, 2025

The JCA is live

After3 years in the making, the Joint Clinical Assessment for the EU is in effect. From 12th January 2025 new cancer medicines and advanced...

00:25:24Jan 13, 2025

Innovative Treatments for Cutaneous T-Cell Lymphoma with Leonard Mazur of Citius Pharmaceuticals

Welcome to this month's P4A Let’s Talk Rare podcast episode by Partners4Acess . Today, Georgie and Owen are joined by Leonard Mazur , CEO of...

00:26:21Nov 19, 2024

Amplifying Patient Voices: Wes Michael on Rare Disease Advocacy

In this episode of P4A Let's Talk Rare , hosts Georgie and Owen Bryant from Partners For Access are joined by Wes Michael , founder and pres...

00:23:54Oct 10, 2024

Impact of Mergers, Acquisitions, and Patent Expirations on Job Cuts in Pharma and Biotech: Insights from Aurelija Luko and Darren Callanan

Welcome to this month's episode of the P4A Let’s Talk Rare podcast by Partners4Acess. Today, Georgie and Owen are joined by their colleagues...

00:27:15Jul 2, 2024